4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
6 companies found
47 approved / 88 designated
9 approved / 23 designated
11 designated · 0 approved
6 designated · 0 approved
1 approved / 2 designated
1 designated · 0 approved