2
Orphan Designations
0
FDA Approvals
4
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| DYRK1A-related intellectual disability syndrome | Cells produced using the AastromReplicelle System and SC-I Therapy Kit | Orphan Designation | - |
| anosmia for isobutyric acid | Cells produced using the AastromReplicelle System and SC-I Therapy Kit | Orphan Designation | - |
| neuroacanthocytosis | Cells produced using the AastromReplicelle System and SC-I Therapy Kit | Orphan Designation | - |
| osteonecrosis | Tissue repair cells obtained from autologous bone marrow expanded ex vivo with a cell production system | Orphan Designation | - |