7
Orphan Designations
0
FDA Approvals
11
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| NPHP3-related Meckel-like syndrome | masitinib | Orphan Designation | - |
| acute myeloid leukemia | 1-{4-[2-(5-ethoxymethyl-2-methyl-phenylamino)-oxazol-5-yl]-phenyl}-imidazolidin-2-one | Orphan Designation | - |
| amyotrophic lateral sclerosis | masitinib mesylate | Orphan Designation | - |
| digestive system cancer | masitinib | Orphan Designation | - |
| digestive system neuroendocrine tumor, grade 1/2 | masitinib | Orphan Designation | - |
| gastric cancer | masitinib mesylate | Orphan Designation | - |
| mastocytosis | masitinib | Orphan Designation | - |
| pancreatic hypoplasia-diabetes-congenital heart disease syndrome | masitinib | Orphan Designation | - |
| pheochromocytoma/paraganglioma syndrome 4 | masitinib | Orphan Designation | - |
| plasma cell myeloma | N-(methyl-diazacyclohexyl-methylbenzamide)-azaphenyl-aminothiopyrrole) mesylate | Orphan Designation | - |
| thrombocytopenia-absent radius syndrome | masitinib | Orphan Designation | - |