1
Orphan Designations
0
FDA Approvals
6
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| COVID-19–associated multisystem inflammatory syndrome in children | Lupron Depot-Ped | Orphan Designation | - |
| bilirubin encephalopathy | Lupron Depot-Ped | Orphan Designation | - |
| central precocious puberty | Lupron Depot-Ped | Orphan Designation | - |
| febrile infection-related epilepsy syndrome | Lupron Depot-Ped | Orphan Designation | - |
| nut midline carcinoma | Lupron Depot-Ped | Orphan Designation | - |
| spinal muscular atrophy | Lupron Depot-Ped | Orphan Designation | - |