1
Orphan Designations
0
FDA Approvals
11
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| HELLP syndrome | Zevaskyn | Orphan Designation | - |
| acral dystrophic epidermolysis bullosa | Zevaskyn | Orphan Designation | - |
| centripetalis recessive dystrophic epidermolysis bullosa | Zevaskyn | Orphan Designation | - |
| dystrophic epidermolysis bullosa pruriginosa | Zevaskyn | Orphan Designation | - |
| dystrophic epidermolysis bullosa, nails only | Zevaskyn | Orphan Designation | - |
| generalized dominant dystrophic epidermolysis bullosa | Zevaskyn | Orphan Designation | - |
| localized dystrophic epidermolysis bullosa | Zevaskyn | Orphan Designation | - |
| pediatric hepatocellular carcinoma | Zevaskyn | Orphan Designation | - |
| pretibial dystrophic epidermolysis bullosa | Zevaskyn | Orphan Designation | - |
| recessive dystrophic epidermolysis bullosa | Zevaskyn | Orphan Designation | - |
| recessive dystrophic epidermolysis bullosa-generalized other | Zevaskyn | Orphan Designation | - |