1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| LCAT deficiency | Recombinant human apolipoprotein A-I/phospholipid complexes | Orphan Designation | - |
| Norum disease | Recombinant human apolipoprotein A-I/phospholipid complexes | Orphan Designation | - |
| fish eye disease | Recombinant human apolipoprotein A-I/phospholipid complexes | Orphan Designation | - |