4
Orphan Designations
0
FDA Approvals
6
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| alveolar soft part sarcoma | elraglusib | Orphan Designation | - |
| glioblastoma | 3-(5-Fluoro-benzofuran-3-yl)-4-(5-methyl-5H-[1,3]dioxolo[4,5-f]indol-7-yl)-pyrrole-2,5-dione | Orphan Designation | - |
| malignant pancreatic neoplasm | elraglusib | Orphan Designation | - |
| neuroblastoma | 3-(5-Fluoro-benzofuran-3-yl)-4-(5-methyl-5H-[1,3]dioxolo[4,5 f]indol-7-yl)-pyrrole-2,5-dione | Orphan Designation | - |
| soft tissue sarcoma | elraglusib | Orphan Designation | - |
| undifferentiated pleomorphic sarcoma | elraglusib | Orphan Designation | - |