1
Orphan Designations
0
FDA Approvals
5
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| ciliary dyskinesia, primary, 40 | Gocovri | Orphan Designation | - |
| episodic kinesigenic dyskinesia 1 | Gocovri | Orphan Designation | - |
| paroxysmal nonkinesigenic dyskinesia 1 | Gocovri | Orphan Designation | - |
| primary ciliary dyskinesia 10 | Gocovri | Orphan Designation | - |
| primary ciliary dyskinesia 3 | Gocovri | Orphan Designation | - |