6
Orphan Designations
0
FDA Approvals
7
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Alstrom syndrome | GVAX melanoma | Orphan Designation | - |
| Finnish type amyloidosis | GVAX melanoma | Orphan Designation | - |
| acute myeloid leukemia | Replication-incompetent GM-CSF-expressing gene-modified allogeneic acute myeloid leukemia cancer cell lines | Orphan Designation | - |
| chronic myelogenous leukemia, BCR-ABL1 positive | Replication-incompetent GM-CSF-expressing gene-modified allogeneic chronic myeloid leukemia cancer cell lines | Orphan Designation | - |
| lysinuric protein intolerance | GVAX melanoma | Orphan Designation | - |
| malignant pancreatic neoplasm | listeria monocytogenesReplication-incompetent GM-CSF-expressing gene-modified allogeneic pancreatic cancer cell lines | Orphan Designation | - |
| mesothelioma | Live-attenuated Listeria monocytogenes actA/inlB/human mesothelin (hMeso) Strain hMeso38 | Orphan Designation | - |