15
Orphan Designations
0
FDA Approvals
19
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Bicervical bicornuate uterus with patent cervix and vagina | L-3,4-Dihydroxy-6-[18F]fluorophenylalanine | Orphan Designation | - |
| Ewing sarcoma | Cu-64 anti CD99 | Orphan Designation | - |
| aromatic L-amino acid decarboxylase deficiency | 6-[18F] fluoro-L-m-tyrosine | Orphan Designation | - |
| carbon monoxide-induced delayed encephalopathy | L-3,4-Dihydroxy-6-[18F]fluorophenylalanine6-fluoro-(18F)-L-3,4-dihydroxyphenylalanineTheranost 68Ga RGDtheranost 68Ga-RGD | Orphan Designation | - |
| glioma | 1-(2-Nitro-imidazolyl)-3-[18F]fluoro-2-propanol; 1H-1-(3-[18F]fluoro-2-hydroxypropyl0-2-nitroimidazole (18F-Misonidazole) | Orphan Designation | - |
| glioma susceptibility 1 | Ac-225 alphavbeta3-IAC | Orphan Designation | - |
| hepatoblastoma | [11C]Acetic Acid | Orphan Designation | - |
| medulloblastoma | 2-Amino-4-[11C]methylsulfanyl-butanoic acid, l-[S methyl[11C]methionine | Orphan Designation | - |
| multiple system atrophy | 18Fluorine-N-3-Fluoropropyl-2beta-carbomethoxy-3beta-(4-iodophenyl) Nortropane | Orphan Designation | - |
| multiple system atrophy, cerebellar type | 18Fluorine-N-3-Fluoropropyl-2beta-carbomethoxy-3beta-(4-iodophenyl) Nortropane | Orphan Designation | - |
| multiple system atrophy, parkinsonian type | 18Fluorine-N-3-Fluoropropyl-2beta-carbomethoxy-3beta-(4-iodophenyl) Nortropane | Orphan Designation | - |
| multisystemic smooth muscle dysfunction syndrome | 6-fluoro-(18F)-L-3,4-dihydroxyphenylalanineTheranost 68Ga RGDtheranost 68Ga-RGD | Orphan Designation | - |
| natal teeth-intestinal pseudoobstruction-patent ductus syndrome | L-3,4-Dihydroxy-6-[18F]fluorophenylalanine6-fluoro-(18F)-L-3,4-dihydroxyphenylalanineTheranost 68Ga RGDtheranost 68Ga-RGD | Orphan Designation | - |
| neuroblastoma | Gallium-68 DOTANOC | Orphan Designation | - |
| retinopathy of prematurity | 3-[3-(6-guanidino-1-oxoisoindolin-2yl) propanamido]-3-(pyridine-3yl) propanoic acid dihydrochloride | Orphan Designation | - |
| rhabdoid tumor | O-18F-fluoroethyl-L-tyrosine | Orphan Designation | - |
| rhabdoid tumor of the kidney | O-18F-fluoroethyl-L-tyrosine | Orphan Designation | - |
| rhabdoid tumor predisposition syndrome 1 | O-18F-fluoroethyl-L-tyrosine | Orphan Designation | - |
| soft tissue sarcoma | 1-(2-Nitro-imidazolyl)-3-[18F]fluoro-2-propanol;1H-1-(3-[18F]fluoro-2-hydroxypropyl)-2-nitroimidazole | Orphan Designation | - |