2
Orphan Designations
0
FDA Approvals
4
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| cystic fibrosis | nitric oxide | Orphan Designation | - |
| non-Zellweger spectrum disorder | Nitric oxide | Orphan Designation | - |
| non-eruption of teeth-maxillary hypoplasia-genu valgum syndrome | Nitric oxide | Orphan Designation | - |
| pulmonary non-tuberculous mycobacterial infection | Nitric oxide | Orphan Designation | - |