1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| facial dermoid cyst | rapamycin | Orphan Designation | - |
| juvenile nasopharyngeal angiofibroma | rapamycin | Orphan Designation | - |
| persistent idiopathic facial pain | rapamycin | Orphan Designation | - |