1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Dorfman-Chanarin disease | D-beta-hydroxybutyrate | Orphan Designation | - |
| disorder of fatty acid oxidation and ketogenesis | D-beta-hydroxybutyrate | Orphan Designation | - |
| inherited fatty acid metabolism disorder | D-beta-hydroxybutyrate | Orphan Designation | - |