1
Orphan Designations
2
FDA Approvals
6
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| recurrent acute pancreatitis | Vowst | Orphan Designation | - |
| recurrent hypersomnia | Vowst | Orphan Designation | - |
| recurrent idiopathic neuroretinitis | Vowst | Orphan Designation | - |
| recurrent metabolic encephalomyopathic crises-rhabdomyolysis-cardiac arrhythmia-intellectual disability syndrome | Vowst | Orphan Designation | - |
| recurrent respiratory papillomatosis | Vowst | Orphan Designation | - |
| twin to twin transfusion syndrome | Vowst | Orphan Designation | - |