2
Orphan Designations
0
FDA Approvals
4
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Dubowitz syndrome | humanized connexin 43 monoclonal antibody | Orphan Designation | - |
| acute disseminated encephalomyelitis | humanized connexin 43 monoclonal antibody | Orphan Designation | - |
| osteosarcoma | Humanized connexin 43 (hCx43) monoclonal antibody | Orphan Designation | - |
| spinal muscular atrophy, distal, autosomal recessive, 6 | humanized connexin 43 monoclonal antibody | Orphan Designation | - |