1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| idiopathic neonatal atrial flutter | lentiviral vector expressing native surfactant protein B | Orphan Designation | - |
| neonatal antiphospholipid syndrome | lentiviral vector expressing native surfactant protein B | Orphan Designation | - |
| surfactant metabolism dysfunction, pulmonary, 1 | lentiviral vector expressing native surfactant protein B | Orphan Designation | - |