2
Orphan Designations
0
FDA Approvals
14
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Aicardi syndrome | Doxil | Orphan Designation | - |
| autosomal dominant osteosclerosis, Worth type | Doxil | Orphan Designation | - |
| clear cell renal carcinoma | Doxil | Orphan Designation | - |
| cleft soft palate | Doxil | Orphan Designation | - |
| interstitial cystitis | Elmiron | Orphan Designation | - |
| metastatic carcinoma | Doxil | Orphan Designation | - |
| metastatic carcinoma in the adrenal medulla | Doxil | Orphan Designation | - |
| metastatic carcinoma in the bone | Doxil | Orphan Designation | - |
| multiple sclerosis | Elmiron | Orphan Designation | - |
| ovarian cancer | Doxil | Orphan Designation | - |
| platinum-induced ototoxicity | Doxil | Orphan Designation | - |
| primary progressive multiple sclerosis | Elmiron | Orphan Designation | - |
| progressive relapsing multiple sclerosis | Elmiron | Orphan Designation | - |
| secondary progressive multiple sclerosis | Elmiron | Orphan Designation | - |