0
Orphan Designations
3
FDA Approvals
Latest: OPFOLDA (2023)
0
Active Trials
0
Rare Diseases
1
News (30d)
AMICUS THERAPEUTICS US, LLC is a company with 0 orphan drug designations across 0 rare diseases, including 3 FDA-approved therapies. 1 news article in the past 30 days.
Disease-by-disease pipeline progression from orphan designation through clinical trials to FDA approval.
Source: FDA Orphan Drug Designations, ClinicalTrials.gov, Drugs@FDA
No pipeline data available yet.