1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Dubowitz syndrome | FGFR and ITGB1 agonist peptide amphiphile scaffold | Orphan Designation | - |
| acute disseminated encephalomyelitis | FGFR and ITGB1 agonist peptide amphiphile scaffold | Orphan Designation | - |
| spinal muscular atrophy, distal, autosomal recessive, 6 | FGFR and ITGB1 agonist peptide amphiphile scaffold | Orphan Designation | - |