1
Orphan Designations
0
FDA Approvals
5
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| acute flaccid myelitis | Histrelin | Orphan Designation | - |
| acute intermittent porphyria | Histrelin | Orphan Designation | - |
| acute lymphoblastic leukemia | Histrelin | Orphan Designation | - |
| porphyria, acute intermittent, nonerythroid variant | Histrelin | Orphan Designation | - |
| variegate porphyria | Histrelin | Orphan Designation | - |