1
Orphan Designations
0
FDA Approvals
2
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| congenital hereditary endothelial dystrophy of cornea | Recombinant Adeno-Associated Virus 8 vector encoding human solute carrier family 4 member 11 variant B protein | Orphan Designation | - |
| congenital hereditary endothelial dystrophy type I | Recombinant Adeno-Associated Virus 8 vector encoding human solute carrier family 4 member 11 variant B protein | Orphan Designation | - |