3
Orphan Designations
0
FDA Approvals
15
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Clostridium difficile colitis | metronidazole | Orphan Designation | - |
| Clostridium infectious disease | metronidazole | Orphan Designation | - |
| T-cell acute lymphoblastic leukemia | paromomycin sulfate/gentamicin sulfate | Orphan Designation | - |
| acute lymphoblastic leukemia | paromomycin sulfate/gentamicin sulfate | Orphan Designation | - |
| adult acute lymphoblastic leukemia | paromomycin sulfate/gentamicin sulfate | Orphan Designation | - |
| bullous pemphigoid | paromomycin sulfate/gentamicin sulfate | Orphan Designation | - |
| childhood acute lymphoblastic leukemia | paromomycin sulfate/gentamicin sulfate | Orphan Designation | - |
| cutaneous leishmaniasis | paromomycin | Orphan Designation | - |
| leishmaniasis | paromomycin | Orphan Designation | - |
| leishmaniasis, diffuse cutaneous | paromomycin | Orphan Designation | - |
| mucocutaneous leishmaniasis | paromomycin | Orphan Designation | - |
| new-onset refractory status epilepticus | paromomycin | Orphan Designation | - |
| primary cutaneous lymphoma | paromomycin | Orphan Designation | - |
| salivary substance, Clostridium botulinum type | metronidazole | Orphan Designation | - |
| teeth, odd shapes of | paromomycin sulfate/gentamicin sulfate | Orphan Designation | - |