2
Orphan Designations
0
FDA Approvals
2
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| epidermolysis bullosa | Hypotonic, acid oxidizing solution containing hypochlorous acid (HClO) | Orphan Designation | - |
| phenylketonuria | L-serine, L-threonine, L-leucine, glycine, L-alanine, L-arginine, L-cysteine, L-glutamine, L-histidine, L-aspartic acid, L-proline, L-isoleucine, L-lysine, L-tryptophan, L-valine, L-methionine, L-tyrosine, carnitine and taurine | Orphan Designation | - |