2
Orphan Designations
0
FDA Approvals
6
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Char syndrome | URSO 250 | Orphan Designation | - |
| aldosterone-producing adenoma with seizures and neurological abnormalities | URSO 250 | Orphan Designation | - |
| ciliary dyskinesia, primary, 40 | URSO 250 | Orphan Designation | - |
| pediatric hepatocellular carcinoma | beclomethasone | Orphan Designation | - |
| pediatric ovarian dysgerminoma | beclomethasone | Orphan Designation | - |
| pediatric-onset Graves disease | beclomethasone | Orphan Designation | - |