2
Orphan Designations
0
FDA Approvals
4
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| familial Mediterranean fever | Colcrys | Orphan Designation | - |
| malaria | quinine Sulfate | Orphan Designation | - |
| polysyndactyly 4 | quinine Sulfate | Orphan Designation | - |
| pure hereditary spastic paraplegia | quinine Sulfate | Orphan Designation | - |