1
Orphan Designations
0 approved, 1 designated
2
FDA Approvals
Latest: XPHOZAH 10 MG (2023)
0
Active Trials
3
Rare Diseases
across 7 areas
0
News (30d)
Quiet
Ardelyx, Inc. is a company with 1 orphan drug designation across 3 rare diseases, including 2 FDA-approved therapies.
Disease-by-disease pipeline progression from orphan designation through clinical trials to FDA approval.
Source: FDA Orphan Drug Designations, ClinicalTrials.gov, Drugs@FDA
| Disease | Drug(s) | Stage |
|---|---|---|
| pediatric hepatocellular carcinoma | tenapanor hydrochloride | Des.TrialAppr. |
| pediatric ovarian dysgerminoma | tenapanor hydrochloride | Des.TrialAppr. |
| pediatric-onset Graves disease | tenapanor hydrochloride | Des.TrialAppr. |
0% of portfolio targets high unmet need diseases
77
overlap in 2+ diseases
0/3
candidate diseases
0
avg importance: 0
0
affecting portfolio
0% of portfolio targets high unmet need diseases
77
overlap in 2+ diseases
0/3
candidate diseases
0
avg importance: 0
0
affecting portfolio