4
Orphan Designations
0 approved, 4 designated
0
FDA Approvals
0
Active Trials
4
Rare Diseases
across 9 areas
0
News (30d)
Quiet
AROG Pharmaceuticals, LLC is a company with 4 orphan drug designations across 4 rare diseases.
Disease-by-disease pipeline progression from orphan designation through clinical trials to FDA approval.
Source: FDA Orphan Drug Designations, ClinicalTrials.gov, Drugs@FDA
| Disease | Drug(s) | Stage |
|---|---|---|
| acute myeloid leukemia | crenolanib | Des.TrialAppr. |
| gastric cancer | crenolanib | Des.TrialAppr. |
| malignant glioma | crenolanib besylate | Des.TrialAppr. |
| soft tissue sarcoma | crenolanib | Des.TrialAppr. |
0% of portfolio targets high unmet need diseases
34
overlap in 2+ diseases
0/4
candidate diseases
0
avg importance: 0
0
affecting portfolio
0% of portfolio targets high unmet need diseases
34
overlap in 2+ diseases
0/4
candidate diseases
0
avg importance: 0
0
affecting portfolio