1
Orphan Designations
0
FDA Approvals
6
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| LEOPARD syndrome 3 | Braftovi | Orphan Designation | - |
| Noonan syndrome 7 | Braftovi | Orphan Designation | - |
| adult-onset non-insulinoma persistent hyperinsulinemic hypoglycemia | Braftovi | Orphan Designation | - |
| cardiofaciocutaneous syndrome 1 | Braftovi | Orphan Designation | - |
| lung cancer | Braftovi | Orphan Designation | - |
| pleomorphic xanthoastrocytoma BRAF mutant | Braftovi | Orphan Designation | - |