1
Orphan Designations
0 approved, 1 designated
1
FDA Approvals
Latest: ESTROGEL (2004)
1
Active Trials
173 recruiting
4
Rare Diseases
across 9 areas
0
News (30d)
Quiet
ASCEND Therapeutics US, LLC is a company with 1 orphan drug designation across 4 rare diseases, including 1 FDA-approved therapy. Active clinical trials in 1 indication. gene therapy candidates in 1 disease.
Disease-by-disease pipeline progression from orphan designation through clinical trials to FDA approval.
Source: FDA Orphan Drug Designations, ClinicalTrials.gov, Drugs@FDA
| Disease | Drug(s) | Stage |
|---|---|---|
| estrogen resistance syndrome | estradiol Gel | Des.TrialAppr. |
| estrogen-receptor negative breast cancer | estradiol Gel | Des.TrialAppr. |
| estrogen-receptor positive breast cancer | estradiol Gel | Des.TrialAppr. |
| hemophilia A | - | Des.TrialAppr. |
0% of portfolio targets high unmet need diseases
0
overlap in 2+ diseases
1/4
candidate diseases
0
avg importance: 0
0
affecting portfolio
0% of portfolio targets high unmet need diseases
0
overlap in 2+ diseases
1/4
candidate diseases
0
avg importance: 0
0
affecting portfolio