1
Orphan Designations
0
FDA Approvals
4
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Dubowitz syndrome | Yorvipath | Orphan Designation | - |
| Kabuki syndrome 1 | Yorvipath | Orphan Designation | - |
| hypoparathyroidism | Yorvipath | Orphan Designation | - |
| metaphyseal chondrodysplasia, Jansen type | Yorvipath | Orphan Designation | - |