3
Orphan Designations
0
FDA Approvals
9
Rare Diseases
2
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| acute cor pulmonale | Meropenem | Orphan Designation | - |
| acute interstitial pneumonia | Meropenem | Orphan Designation | - |
| adult neuronal ceroid lipofuscinosis | Imfinzi | Orphan Designation | - |
| adult pleomorphic rhabdomyosarcoma | Imfinzi | Orphan Designation | - |
| adult-onset non-insulinoma persistent hyperinsulinemic hypoglycemia | Imfinzi | Orphan Designation | - |
| adult-onset proximal spinal muscular atrophy, autosomal dominant | Imfinzi | Orphan Designation | - |
| gastric cancer | Imfinzian anti-Claudin 18.2 monoclonal antibody conjugated with MMAE payload | Orphan Designation | - |
| primary adult heart tumor | Imfinzi | Orphan Designation | - |
| toxic pneumonitis | Meropenem | Orphan Designation | - |