2
Orphan Designations
0
FDA Approvals
4
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Hurler syndrome | adult adherent bone marrow-derived multipotent stem cells | Orphan Designation | - |
| Hurler-Scheie syndrome | adult adherent bone marrow-derived multipotent stem cells | Orphan Designation | - |
| Scheie syndrome | adult adherent bone marrow-derived multipotent stem cells | Orphan Designation | - |
| graft versus host disease | Multistem | Orphan Designation | - |