2
Orphan Designations
1
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| tuberous sclerosis | sirolimuseverolimus ointment | Orphan Designation | - |
| tuberous sclerosis 1 | sirolimuseverolimus ointment | Orphan Designation | - |
| tuberous sclerosis 2 | sirolimuseverolimus ointment | Orphan Designation | - |