3
Orphan Designations
0
FDA Approvals
7
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Behcet disease | D-mannose | Orphan Designation | - |
| COG8-congenital disorder of glycosylation | L-fucose | Orphan Designation | - |
| MPI-congenital disorder of glycosylation | D-mannose | Orphan Designation | - |
| PGM1-congenital disorder of glycosylation | D-Galactose | Orphan Designation | - |
| congenital disorder of glycosylation type II | L-fucose | Orphan Designation | - |
| congenital disorder of glycosylation, type IIq | L-fucose | Orphan Designation | - |
| mannose-binding lectin deficiency | D-mannose | Orphan Designation | - |