1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Singleton-Merten syndrome 1 | nevirapine | Orphan Designation | - |
| bone marrow failure syndrome 3 | nevirapine | Orphan Designation | - |
| multiple congenital anomalies-hypotonia-seizures syndrome 2 | nevirapine | Orphan Designation | - |