1
Orphan Designations
0
FDA Approvals
5
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| acute lymphoblastic leukemia | Aucatzyl | Orphan Designation | - |
| ataxia, early-onset, with oculomotor apraxia and hypoalbuminemia | Aucatzyl | Orphan Designation | - |
| autosomal recessive Parkinson disease 14 | Aucatzyl | Orphan Designation | - |
| leukoencephalopathy, diffuse hereditary, with spheroids 1 | Aucatzyl | Orphan Designation | - |
| neuroferritinopathy | Aucatzyl | Orphan Designation | - |