2
Orphan Designations
0
FDA Approvals
14
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| AHDC1-related intellectual disability - obstructive sleep apnea - mild dysmorphism syndrome | XIAFLEX | Orphan Designation | - |
| Peyronie disease | XIAFLEX | Orphan Designation | - |
| adult pleomorphic rhabdomyosarcoma | XIAFLEX | Orphan Designation | - |
| adult-onset non-insulinoma persistent hyperinsulinemic hypoglycemia | XiaflexXIAFLEX | Orphan Designation | - |
| advanced heart failure | Xiaflex | Orphan Designation | - |
| advanced sleep phase syndrome | Xiaflex | Orphan Designation | - |
| advanced sleep phase syndrome 1 | Xiaflex | Orphan Designation | - |
| advanced sleep phase syndrome 2 | Xiaflex | Orphan Designation | - |
| advanced sleep phase syndrome 3 | Xiaflex | Orphan Designation | - |
| gastric cancer | XIAFLEX | Orphan Designation | - |
| hepatocellular carcinoma | XIAFLEX | Orphan Designation | - |
| lethal multiple pterygium syndrome | XIAFLEX | Orphan Designation | - |
| primary adult heart tumor | XIAFLEX | Orphan Designation | - |
| sideroblastic anemia 3 | XIAFLEX | Orphan Designation | - |