2
Orphan Designations
0
FDA Approvals
6
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Crohn disease | quisovalimab | Orphan Designation | - |
| inflammatory bowel disease 1 | quisovalimab | Orphan Designation | - |
| lymphatic malformation | trans-4-[4-Amino-5-(7-methoxy-1H-indol-2-yl)-imidazo[5,1-f][1,2,4]triazine-7-yl]-cyclohexanecarboxylic acid, tromethamine salt | Orphan Designation | - |
| lymphatic malformation 5 | trans-4-[4-Amino-5-(7-methoxy-1H-indol-2-yl)-imidazo[5,1-f][1,2,4]triazine-7-yl]-cyclohexanecarboxylic acid, tromethamine salt | Orphan Designation | - |
| lymphatic malformation 6 | trans-4-[4-Amino-5-(7-methoxy-1H-indol-2-yl)-imidazo[5,1-f][1,2,4]triazine-7-yl]-cyclohexanecarboxylic acid, tromethamine salt | Orphan Designation | - |
| pediatric hepatocellular carcinoma | quisovalimab | Orphan Designation | - |