2
Orphan Designations
0
FDA Approvals
5
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| acute flaccid myelitis | Dimerizing drug that binds to mutated Fas protein/drug-binding domain fusion protein (FKBP) | Orphan Designation | - |
| acute graft versus host disease | Dimerizing drug that binds to mutated Fas protein/drug-binding domain fusion protein (FKBP) | Orphan Designation | - |
| acute lymphoblastic leukemia | Dimerizing drug that binds to mutated Fas protein/drug-binding domain fusion protein (FKBP) | Orphan Designation | - |
| graft versus host disease | CaspaCIDe System (combination product) consisting of allogeneic T Cell genetically modified to contain an inducible caspase 9 gene and Rimiducid | Orphan Designation | - |
| immunodeficiency disease | CaspaCIDe System (combination product) consisting of allogeneic T Cell genetically modified to contain an inducible caspase 9 gene and Rimiducid | Orphan Designation | - |