5
Orphan Designations
1
FDA Approvals
12
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| 15q11q13 microduplication syndrome | Cannabidiol | Orphan Designation | - |
| Angelman syndrome | Cannabidiol | Orphan Designation | - |
| Fanconi anemia | cannabidiol | Orphan Designation | - |
| GM1 gangliosidosis | cannabidiol | Orphan Designation | - |
| Huntington disease | cannabidiol | Orphan Designation | - |
| Malan overgrowth syndrome | cannabidiol | Orphan Designation | - |
| Peters plus syndrome | cannabidiol | Orphan Designation | - |
| childhood absence epilepsy | cannabidiol | Orphan Designation | - |
| chromosome 15q11.2 deletion syndrome | Cannabidiol | Orphan Designation | - |
| duplication/inversion 15q11 | Cannabidiol | Orphan Designation | - |
| infantile spasms | cannabidiol | Orphan Designation | - |
| microphthalmia, syndromic 2 | cannabidiol | Orphan Designation | - |