6
Orphan Designations
0
FDA Approvals
18
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Noonan syndrome 1 | Coagadex | Orphan Designation | - |
| acquired factor X deficiency | Coagulation Factor X Human | Orphan Designation | - |
| acquired thrombotic thrombocytopenic purpura | Gammaplex | Orphan Designation | - |
| acute tricyclic antidepressant poisoning | Alpha-1-acid glycoprotein | Orphan Designation | - |
| arthrogryposis, renal dysfunction, and cholestasis 1 | Coagadex | Orphan Designation | - |
| autoimmune thrombocytopenic purpura | Gammaplex | Orphan Designation | - |
| autosomal recessive distal spinal muscular atrophy 1 | Coagadex | Orphan Designation | - |
| cocaine abuse | Alpha-1-acid glycoprotein | Orphan Designation | - |
| cocaine dependence | Alpha-1-acid glycoprotein | Orphan Designation | - |
| cocaine intoxication | Alpha-1-acid glycoprotein | Orphan Designation | - |
| congenital factor X deficiency | Coagadex | Orphan Designation | - |
| congenital factor XI deficiency | human coagulation factor XI | Orphan Designation | - |
| esophageal varices | Coagadex | Orphan Designation | - |
| hemorrhagic disease of newborn | Coagadex | Orphan Designation | - |
| idiopathic aplastic anemia | Gammaplex | Orphan Designation | - |
| idiopathic disseminated cytomegalovirus infection | Gammaplex | Orphan Designation | - |
| idiopathic hypereosinophilic syndrome | Gammaplex | Orphan Designation | - |
| platelet-type bleeding disorder 19 | Coagadex | Orphan Designation | - |