1
Orphan Designations
0
FDA Approvals
6
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Jeffries-Lakhani neurodevelopmental syndrome | Recombinant human gelsolin | Orphan Designation | - |
| acute disseminated encephalomyelitis | Recombinant human gelsolin | Orphan Designation | - |
| acute flaccid myelitis | Recombinant human gelsolin | Orphan Designation | - |
| acute lymphoblastic leukemia | Recombinant human gelsolin | Orphan Designation | - |
| acute myeloid leukemia | Recombinant human gelsolin | Orphan Designation | - |
| respiratory failure | Recombinant human gelsolin | Orphan Designation | - |