1
Orphan Designations
0
FDA Approvals
5
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Aarskog-Scott syndrome, X-linked | Orlaam | Orphan Designation | - |
| RAB23-related Carpenter syndrome | Orlaam | Orphan Designation | - |
| autosomal recessive faciodigitogenital syndrome | Orlaam | Orphan Designation | - |
| mucopolysaccharidosis type 7 | Orlaam | Orphan Designation | - |
| opiate dependence | Orlaam | Orphan Designation | - |