1
Orphan Designations
0
FDA Approvals
6
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Noonan syndrome 8 | Temoporfin | Orphan Designation | - |
| recurrent acute pancreatitis | Temoporfin | Orphan Designation | - |
| recurrent hypersomnia | Temoporfin | Orphan Designation | - |
| recurrent idiopathic neuroretinitis | Temoporfin | Orphan Designation | - |
| recurrent metabolic encephalomyopathic crises-rhabdomyolysis-cardiac arrhythmia-intellectual disability syndrome | Temoporfin | Orphan Designation | - |
| recurrent respiratory papillomatosis | Temoporfin | Orphan Designation | - |