2
Orphan Designations
0
FDA Approvals
6
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| antibody mediated epilepsy | riliprubart | Orphan Designation | - |
| autoimmune hemolytic anemia | a humanized IgG4 monoclonal antibody, produced in CHO cells, that binds to and inhibits the activated form of the classical complement pathway (CP) specific serine protease, C1s | Orphan Designation | - |
| mixed-type autoimmune hemolytic anemia | a humanized IgG4 monoclonal antibody, produced in CHO cells, that binds to and inhibits the activated form of the classical complement pathway (CP) specific serine protease, C1s | Orphan Designation | - |
| myelin oligodendrocyte glycoprotein antibody-associated disease | riliprubart | Orphan Designation | - |
| non-autoimmune hemolytic anemia | a humanized IgG4 monoclonal antibody, produced in CHO cells, that binds to and inhibits the activated form of the classical complement pathway (CP) specific serine protease, C1s | Orphan Designation | - |
| platelet abnormalities with eosinophilia and immune-mediated inflammatory disease | riliprubart | Orphan Designation | - |