2
Orphan Designations
0
FDA Approvals
11
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Huntington disease | iobenguane sulfate I-123Iobenguane Sulfate I-123 | Orphan Designation | - |
| Wolf-Hirschhorn syndrome | iobenguane sulfate I-123 | Orphan Designation | - |
| anosmia for isobutyric acid | Iobenguane Sulfate I-123 | Orphan Designation | - |
| chromosome 15q26-qter deletion syndrome | iobenguane sulfate I-123 | Orphan Designation | - |
| chromosome 18p deletion syndrome | iobenguane sulfate I-123 | Orphan Designation | - |
| chromosome 1q21.1 deletion syndrome | iobenguane sulfate I-123 | Orphan Designation | - |
| developmental and epileptic encephalopathy, 57 | Iobenguane Sulfate I-123 | Orphan Designation | - |
| double nail for fifth toe | Iobenguane Sulfate I-123 | Orphan Designation | - |
| modifier, X-linked, for Neurofunctional defects | Iobenguane Sulfate I-123 | Orphan Designation | - |
| spatial visualization, aptitude for | Iobenguane Sulfate I-123 | Orphan Designation | - |
| thrombocytopenia-absent radius syndrome | iobenguane sulfate I-123 | Orphan Designation | - |