6
Orphan Designations
0
FDA Approvals
18
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| AIDS related complex | Interferon alfa-nl | Orphan Designation | - |
| AIDS-related disorder | Interferon alfa-nl | Orphan Designation | - |
| Chagas disease | Allopurinol riboside | Orphan Designation | - |
| Kaposi's sarcoma | Interferon alfa-nl | Orphan Designation | - |
| breast fibrocystic disease | Allopurinol riboside | Orphan Designation | - |
| carcinoma ex pleomorphic adenoma | Allopurinol sodium | Orphan Designation | - |
| chlamydiaceae infections | Piritrexim isethionate | Orphan Designation | - |
| deltaretrovirus infections | Piritrexim isethionate | Orphan Designation | - |
| major salivary gland carcinoma ex pleomorphic adenoma | Allopurinol sodium | Orphan Designation | - |
| parotid gland carcinoma ex pleomorphic adenoma | Allopurinol sodium | Orphan Designation | - |
| rheumatic disease of mitral valve | Allopurinol riboside | Orphan Designation | - |
| severe Canavan disease | Gancyclovir | Orphan Designation | - |
| severe achondroplasia-developmental delay-acanthosis nigricans syndrome | Gancyclovir | Orphan Designation | - |
| severe intellectual disability-poor language-strabismus-grimacing face-long fingers syndrome | Gancyclovir | Orphan Designation | - |
| short stature-webbed neck-heart disease syndrome | Allopurinol riboside | Orphan Designation | - |
| sickle cell disease | substituted benzaldehyde that binds to the oxy-conformation of Hb between amino terminal residues of the alpha-subunits | Orphan Designation | - |
| spirochaetales infections | Piritrexim isethionate | Orphan Designation | - |
| visceral leishmaniasis | Allopurinol riboside | Orphan Designation | - |