2
Orphan Designations
0
FDA Approvals
2
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| plasma cell myeloma | a new chemical entity that binds to cereblon, an E3 ligase, enabling the recruitment and degradation of IKAROS Family Zinc Finger proteins 1 and 3 (IKZF1/3) | Orphan Designation | - |
| soft tissue sarcoma | small molecule composed of a ligand binding moiety to BRD9, a chemical linker, and a ligand binding moiety to the cereblon (CRBN) E3 ligase | Orphan Designation | - |