1
Orphan Designations
0
FDA Approvals
6
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| cardiomyopathy, familial hypertrophic, 28 | Pramiracetam Sulfate | Orphan Designation | - |
| epilepsy, familial adult myoclonic, 1 | Pramiracetam Sulfate | Orphan Designation | - |
| epilepsy, familial adult myoclonic, 2 | Pramiracetam Sulfate | Orphan Designation | - |
| epilepsy, familial adult myoclonic, 3 | Pramiracetam Sulfate | Orphan Designation | - |
| epilepsy, familial adult myoclonic, 4 | Pramiracetam Sulfate | Orphan Designation | - |
| multiple mitochondrial dysfunctions syndrome 3 | Pramiracetam Sulfate | Orphan Designation | - |