4
Orphan Designations
0
FDA Approvals
13
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Bloom syndrome | VARIZIG | Orphan Designation | - |
| Bruton-type agammaglobulinemia | HepaGam B | Orphan Designation | - |
| botulism | botulism antitoxin heptavalent (A, B, C, D, E, F, G) (Equine) | Orphan Designation | - |
| hereditary spastic paraplegia 23 | VARIZIG | Orphan Designation | - |
| isotretinoin syndrome | VARIZIG | Orphan Designation | - |
| lymphoproliferative syndrome 2 | VARIZIG | Orphan Designation | - |
| major depressive disorder | CNJ-016 | Orphan Designation | - |
| malignant carotid body paraganglioma | CNJ-016 | Orphan Designation | - |
| microvascular complications of diabetes, susceptibility | CNJ-016 | Orphan Designation | - |
| post 5-alpha-reductase inhibitors treatment syndrome | CNJ-016 | Orphan Designation | - |
| post-treatment Lyme disease syndrome | CNJ-016 | Orphan Designation | - |
| treatment-refractory schizophrenia | CNJ-016 | Orphan Designation | - |
| varicella, severe recurrent | VARIZIG | Orphan Designation | - |